Delivering genes to a subset of cells can lead to those cells delivering proteins more broadly, potentially affecting the whole body.

“And the advantage that we don't yet have a good way of delivering to every cell in the body or every stem cell in the body. Remember I said delivery was very important and it's so important. We need to fix it. But anyway, in the meantime, we can deliver the genes to a subset of cells in various parts of the body, and then those subset will deliver the proteins, those three proteins you mentioned, more broadly. And so you can, in principle, affect the whole body by that combination of two kind of tiers of delivery. That's the idea behind that.”