Gene therapies, such as SPARC Therapeutics' drug for retinal degeneration, can cost hundreds of thousands of dollars per treatment.

“The use of gene therapy, putting in a missing gene, and, in fact, editing for that matter for rare genetic diseases is by its nature expensive. It's millions of dollars per person over a lifetime, partly because the R&D costs and the palliative care and all sorts of health care for someone who has a very severe disease that might have died young years ago, but thanks to the Orphan Drug Act and others, they can now lead closer to normal life but at millions of dollars.”